neurology 2022 Annual SMA Research & Clinical Care Meeting June 16-19, 2022 — Anaheim, California State of SMA Report Confirms Large Treatment-Related Improvements in Spinal Muscular Atrophy Outcomes Download 4 PowerPoint slides
neurology American Academy of Neurology (AAN) Annual Meeting 2022: Expert Interview Dr. Nicolas Chrestian — Length: 03:26 RESTORE Registry Update: Real-world Benefit for Pre-symptomatic and Older Children Watch Presentation
neurology American Academy of Neurology (AAN) Annual Meeting 2022 April 2-7, 2022 — Seattle, Washington Gene Replacement Therapy Found to be Safe and Effective in Older Patients with Spinal Muscular Atrophy Download 3 PowerPoint slides
neurology 2022 MDA Clinical & Scientific Conference: Expert Interview Dr. Alex MacKenzie — Length: 06:30 Pre-symptomatic Gene Replacement Therapy Transforms the Prognosis of SMA Watch Presentation
neurology 2022 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference March 13-16, 2022 — Nashville, Tennessee & Virtual Gene Replacement Therapy for Spinal Muscular Atrophy Associated with Normal Development Download 4 PowerPoint slides
rheumatology American College of Rheumatology (ACR) Convergence 2021: Expert Interview Dr. Johannes Roth — Length: 07:49 JUNIPERA Trial: Efficacy & Safety of IL-17i in Pediatric Use Watch Presentation
rheumatology American College of Rheumatology (ACR) Convergence 2021 November 5-9, 2021 — Virtual Meeting IL-17 Inhibitor Demonstrates Efficacy in Pediatric Counterparts of nr-axSpA and PsA Download 4 PowerPoint slides
neurology World Muscle Society (WMS) 2021 Virtual Congress September 20-24, 2021 — Virtual Meeting Gene Replacement Therapy for SMA is Effective in Both Pre-symptomatic Infants and Older Symptomatic Children Download 4 PowerPoint slides
neurology 7th Congress of the European Academy of Neurology (EAN) - Virtual 2021 June 19-22, 2021 — Virtual Meeting STR1VE-EU: Gene Replacement Therapy in Symptomatic Spinal Muscular Atrophy Is Associated with Substantial Benefit Download 4 PowerPoint slides
neurology CURE SMA: Research and Clinical Care Meeting 2021 June 9-11, 2021 — Virtual Meeting Gene Therapy for Spinal Muscular Atrophy Effective as First- or Second-line Therapy Download 4 PowerPoint slides
neurology American Academy of Neurology (AAN) Annual Meeting 2021 April 17-22, 2021 — Virtual Meeting Efficacy of Spinal Muscular Atrophy Therapies Depends on Early Initiation Download 5 PowerPoint slides
neurology Muscular Dystrophy Association (MDA) Conference 2021: Expert Interview Dr. Alex MacKenzie — Length: 07:02 Efficacy of SMN1 Gene Therapy in SMA: Clinical Takeaways from the SPR1NT Trial Watch Presentation